ALNY · SELECTED REGISTRY STUDY
Alnylam Pharmaceuticals
Vutrisiran · NCT04153149
Transthyretin Amyloidosis (ATTR) With Cardiomyopathy
Identity verified 2026-09-26. Latest collection availability appears in your study desk.
Registry study list as of Sep 26, 2026. For current SEC-sourced timing by company, see Companies A–Z.
50 companies · 50 selected studies as of on the daily collection schedule. Search by ticker, company, drug, disease or NCT ID.
One selected study per company. Open a company to read its available sources, or keep a study in your watchlist.
50 studies shown as of
ALNY · SELECTED REGISTRY STUDY
Vutrisiran · NCT04153149
Transthyretin Amyloidosis (ATTR) With Cardiomyopathy
Identity verified 2026-09-26. Latest collection availability appears in your study desk.
IONS · SELECTED REGISTRY STUDY
ION363 (ulefnersen) · NCT04768972
Amyotrophic Lateral Sclerosis
Identity verified 2026-09-26. Latest collection availability appears in your study desk.
LLY · SELECTED REGISTRY STUDY
Donanemab · NCT04437511
Alzheimer Disease
Identity verified 2026-09-26. Latest collection availability appears in your study desk.
VKTX · SELECTED REGISTRY STUDY
VK2735 subcutaneous · NCT07104383
Weight Loss
Identity verified 2026-09-26. Latest collection availability appears in your study desk.
REGN · SELECTED REGISTRY STUDY
Odronextamab · NCT06091865
Diffuse Large B-cell Lymphoma (DLBCL)
Identity verified 2026-09-26. Latest collection availability appears in your study desk.
VRTX · SELECTED REGISTRY STUDY
VX-272 · NCT07437105
Cystic Fibrosis
Identity verified 2026-09-26. Latest collection availability appears in your study desk.
GILD · SELECTED REGISTRY STUDY
Seladelpar · NCT07841977
Primary Biliary Cholangitis
Identity verified 2026-09-26. Latest collection availability appears in your study desk.
AMGN · SELECTED REGISTRY STUDY
Xaluritamig · NCT07297979
Ewing Sarcoma
Identity verified 2026-09-26. Latest collection availability appears in your study desk.
BIIB · SELECTED REGISTRY STUDY
Litifilimab · NCT05531565
Subacute Cutaneous Lupus Erythematosus
Identity verified 2026-09-26. Latest collection availability appears in your study desk.
BMRN · SELECTED REGISTRY STUDY
BMN 333 · NCT07441876
Achondroplasia
Identity verified 2026-09-26. Latest collection availability appears in your study desk.
SRPT · SELECTED REGISTRY STUDY
delandistrogene moxeparvovec · NCT04626674
Duchenne Muscular Dystrophy
Identity verified 2026-09-26. Latest collection availability appears in your study desk.
NBIX · SELECTED REGISTRY STUDY
NBI-1117568 · NCT07105098
Schizophrenia
Identity verified 2026-09-26. Latest collection availability appears in your study desk.
INCY · SELECTED REGISTRY STUDY
INCB161734 · NCT07522073
Solid Tumors
Identity verified 2026-09-26. Latest collection availability appears in your study desk.
EXEL · SELECTED REGISTRY STUDY
Zanzalintinib · NCT07750158
Colorectal Cancer
Identity verified 2026-09-26. Latest collection availability appears in your study desk.
ARGX · SELECTED REGISTRY STUDY
ARGX-117 · NCT05907096
Delayed Graft Function
Identity verified 2026-09-26. Latest collection availability appears in your study desk.
MRNA · SELECTED REGISTRY STUDY
mRNA-1469 · NCT07737717
Ebola-Bundibugyo Virus Disease (Ebola-BDBV)
Identity verified 2026-09-26. Latest collection availability appears in your study desk.
CRSP · SELECTED REGISTRY STUDY
CTX112 · NCT07804004
Progressive Multiple Sclerosis (PMS)
Identity verified 2026-09-26. Latest collection availability appears in your study desk.
NTLA · SELECTED REGISTRY STUDY
Biological NTLA-2002 · NCT05120830
Hereditary Angioedema
Identity verified 2026-09-26. Latest collection availability appears in your study desk.
BEAM · SELECTED REGISTRY STUDY
BEAM-302 · NCT06389877
Alpha 1-Antitrypsin Deficiency
Identity verified 2026-09-26. Latest collection availability appears in your study desk.
EDIT · SELECTED REGISTRY STUDY
EDIT-301 · NCT05444894
Transfusion Dependent Beta Thalassemia
Identity verified 2026-09-26. Latest collection availability appears in your study desk.
RXRX · SELECTED REGISTRY STUDY
REC-7735 · NCT07819136
Solid Tumors
Identity verified 2026-09-26. Latest collection availability appears in your study desk.
ACAD · SELECTED REGISTRY STUDY
ACP-204 · NCT06159673
Alzheimer's Disease Psychosis
Identity verified 2026-09-26. Latest collection availability appears in your study desk.
AXSM · SELECTED REGISTRY STUDY
Solriamfetol Dose A · NCT07717879
ADHD
Identity verified 2026-09-26. Latest collection availability appears in your study desk.
PTCT · SELECTED REGISTRY STUDY
Sepiapterin · NCT06302348
Phenylketonuria
Identity verified 2026-09-26. Latest collection availability appears in your study desk.
RARE · SELECTED REGISTRY STUDY
UX701 · NCT04884815
Wilson Disease
Identity verified 2026-09-26. Latest collection availability appears in your study desk.
DNLI · SELECTED REGISTRY STUDY
tividenofusp alfa · NCT05371613
Mucopolysaccharidosis II
Identity verified 2026-09-26. Latest collection availability appears in your study desk.
ARWR · SELECTED REGISTRY STUDY
ARO-INHBE · NCT06700538
Obesity
Identity verified 2026-09-26. Latest collection availability appears in your study desk.
KYMR · SELECTED REGISTRY STUDY
KT-621 · NCT07823205
Healthy Participants
Identity verified 2026-09-26. Latest collection availability appears in your study desk.
ARVN · SELECTED REGISTRY STUDY
ARV-806 · NCT07023731
KRAS G12D Mutation
Identity verified 2026-09-26. Latest collection availability appears in your study desk.
CCCC · SELECTED REGISTRY STUDY
Cemsidomide · NCT07280013
Multiple Myeloma (MM)
Identity verified 2026-09-26. Latest collection availability appears in your study desk.
KURA · SELECTED REGISTRY STUDY
Ziftomenib · NCT07007312
Acute Myeloid Leukemia (AML)
Identity verified 2026-09-26. Latest collection availability appears in your study desk.
RVMD · SELECTED REGISTRY STUDY
daraxonrasib · NCT07252232
Pancreatic Cancer
Identity verified 2026-09-26. Latest collection availability appears in your study desk.
SNDX · SELECTED REGISTRY STUDY
Revumenib · NCT07211958
Acute Myeloid Leukemias
Identity verified 2026-09-26. Latest collection availability appears in your study desk.
DYN · SELECTED REGISTRY STUDY
zeleciment basivarsen (DYNE-101) · NCT07486934
Myotonic Dystrophy Type 1 (DM1)
Identity verified 2026-09-26. Latest collection availability appears in your study desk.
XENE · SELECTED REGISTRY STUDY
XEN1101 · NCT05718817
Focal Epilepsy
Identity verified 2026-09-26. Latest collection availability appears in your study desk.
PRAX · SELECTED REGISTRY STUDY
1.0mg/kg/day PRAX-562 · NCT07010471
Developmental and Epileptic Encephalopathy 1
Identity verified 2026-09-26. Latest collection availability appears in your study desk.
TGTX · SELECTED REGISTRY STUDY
Ublituximab · NCT04130997
Relapsing Multiple Sclerosis (RMS)
Identity verified 2026-09-26. Latest collection availability appears in your study desk.
ABCL · SELECTED REGISTRY STUDY
ABCL575 · NCT07108894
Healthy Volunteers
Identity verified 2026-09-26. Latest collection availability appears in your study desk.
RCKT · SELECTED REGISTRY STUDY
RP-A701 is a recombinant viral vector composed of an AAV serotype rh.74 (AAVrh.74) capsid encapsulating the transgene, BCL2-associated Athanogene 3 (BAG3) · NCT07137338
Dilated Cardiomyopathy (DCM)
Identity verified 2026-09-26. Latest collection availability appears in your study desk.
COGT · SELECTED REGISTRY STUDY
bezuclastinib · NCT04996875
Advanced Systemic Mastocytosis (AdvSM)
Identity verified 2026-09-26. Latest collection availability appears in your study desk.
IMNM · SELECTED REGISTRY STUDY
IM-1617 · NCT07578571
Colorectal Cancer
Identity verified 2026-09-26. Latest collection availability appears in your study desk.
JANX · SELECTED REGISTRY STUDY
JANX013 · NCT07813637
Prostate Cancer
Identity verified 2026-09-26. Latest collection availability appears in your study desk.
TCRX · SELECTED REGISTRY STUDY
TSC-101 · NCT07702578
AML
Identity verified 2026-09-26. Latest collection availability appears in your study desk.
VERA · SELECTED REGISTRY STUDY
Atacicept · NCT06983028
pMN
Identity verified 2026-09-26. Latest collection availability appears in your study desk.
ALLO · SELECTED REGISTRY STUDY
ALLO-329 · NCT07085104
Systemic Lupus Erythematosus (With and Without Nephritis)
Identity verified 2026-09-26. Latest collection availability appears in your study desk.
FATE · SELECTED REGISTRY STUDY
FT819 · NCT07570862
Lupus Nephritis
Identity verified 2026-09-26. Latest collection availability appears in your study desk.
RCUS · SELECTED REGISTRY STUDY
Casdatifan · NCT07751250
Healthy Participants
Identity verified 2026-09-26. Latest collection availability appears in your study desk.
MIRM · SELECTED REGISTRY STUDY
Low dose of MRM-3379 · NCT07209462
Fragile X Syndrome
Identity verified 2026-09-26. Latest collection availability appears in your study desk.
MDGL · SELECTED REGISTRY STUDY
Resmetirom · NCT07830758
MASH - Metabolic Dysfunction-Associated Steatohepatitis
Identity verified 2026-09-26. Latest collection availability appears in your study desk.
ANAB · SELECTED REGISTRY STUDY
Rosnilimab · NCT06127043
Ulcerative Colitis
Identity verified 2026-09-26. Latest collection availability appears in your study desk.
Reviewed historical examples: 10 companies, 10 milestones and 24 source records from 2022–2025. Recorded by ORION on September 26, 2026. This is a selected evidence set, not a complete company history or continuous monitoring. Later company disclosures may change the current picture. Publication dates are not ORION detection dates.
This registry collection is separate from the 10 company histories with 24 historical announcement records. It is not whole-company surveillance or 50 validated AI analysis reports. Reviewed changes appear when found; missing data stays unavailable.
Primary completion dates are registry dates, not company promises to publish results. Source collection and human review can be delayed.
Each history connects the same company, medicine and development milestone. A registry date, a different indication or a headline mentioning the same drug is not sufficient evidence of the same milestone. Trial identifiers appear only where the sources establish the link.
“Outcome reported” means the company disclosed a result or action, not that ORION independently verified efficacy or approval. An elapsed target window alone never becomes a broken promise. An unclear window or missing follow-up remains “Not yet verified.” “Mid-year” and similar wording are preserved without inventing a precise date.
Publication dates belong to original documents. “ORION first recorded” is when this historical entry entered our catalog; it is not a claim that we discovered the information before the market. Effective dates can be unavailable. Historic entries can be added later.
Records are retained when corrected. A correction identifies the older entry and the reason. A technical fingerprint can detect changes to a published dataset; it does not prove that a company statement is true, that the collection is complete, or that an independent party timestamped it.
Public corrections log · Read the current catalog manifest · Research methodology. No investment scores, rankings, recommendations, price targets or forecasts.
This is a follow-up research question, not an answered claim or forecast. Later disclosures may not be included in this release.